Breaking Gene Therapy News
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Asia Regulatory Roundup: Korean Gene Therapy Probe Triggers Accusations of Data Fabrication, Lawsuit - Regulatory Focus
Apr 23, 2019 | 19:11 pmAsia Regulatory Roundup: Korean Gene Therapy Probe Triggers Accusations of Data Fabrication, Lawsuit Regulatory FocusWelcome to our Asia Regulatory Roundup, our weekly overview of the top regulatory news in Asia. Korean Gene Therapy Probe Triggers Accusations of Data ...
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This New Technology is Making AAV Gene Therapy a Reality - SelectScience
Apr 23, 2019 | 16:55 pmThis New Technology is Making AAV Gene Therapy a Reality SelectScienceNew 'Dissolvable Microcarriers' are addressing challenges associated with AAV-based gene therapies entering the clinic.
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Novartis' case for innovative gene therapy for spinal muscular atrophy gets stronger - The Pharma Letter
Apr 23, 2019 | 16:46 pmNovartis' case for innovative gene therapy for spinal muscular atrophy gets stronger The Pharma LetterPositive interim results from a Phase III trial evaluating the effect of Novartis' (NOVN: VX) Zolgensma (onasemnogene abeparvovec-xioi; AVXS-101) in Type 1 ...
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Foundation Fighting Blindness to Host 6th Annual Retinal Cell & Gene Therapy Innovation Summit Before ARVO - BioSpace
Apr 23, 2019 | 14:01 pmFoundation Fighting Blindness to Host 6th Annual Retinal Cell & Gene Therapy Innovation Summit Before ARVO BioSpacePublished: Apr 23, 2019. The Summit, which will bring physicians, scientists, and industry together to collaboratively advance innovation for emerging retinal ...
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Novartis Says Baby's Death May Be Tied to Gene Therapy - Bloomberg
Apr 23, 2019 | 08:50 amNovartis Says Baby's Death May Be Tied to Gene Therapy BloombergSecond death in gene therapy trial prompts investigation pharmaphorumCan We Afford to Be Cured? A Conversation With ICER's Steve Pearson XconomySecond death in Novartis gene therapy trials under investigation Express BPDView full coverage on Google News
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Doctors use HIV in gene therapy to fix 'bubble boy' disease - Temple Daily Telegram
Apr 23, 2019 | 08:30 amDoctors use HIV in gene therapy to fix 'bubble boy' disease Temple Daily TelegramThey were born without a working germ-fighting system, every infection a threat to their lives. Now eight babies with “bubble boy disease” have had it fixed by a ...
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Mustang Bio soars after its novel gene therapy cured ‘Bubble Boys’ - The Seattle Times
Apr 22, 2019 | 02:00 amMustang Bio soars after its novel gene therapy cured ‘Bubble Boys’ The Seattle TimesShares of the tiny biotechnology company Mustang Bio shot up last week following a scientific breakthrough that cured eight infants suffering from the ...
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Novartis discloses death in European study of gene therapy for SMA - Seeking Alpha
Apr 20, 2019 | 23:06 pmNovartis discloses death in European study of gene therapy for SMA Seeking AlphaOn the heels of its announcement of positive preliminary results from its Phase 3 STR1VE study evaluating gene therapy candidate Zolgensma (onasemnogene ...
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Novartis' star gene therapy faces potential safety issue following a recent infant death in study - Endpoints News
Apr 20, 2019 | 17:12 pmNovartis' star gene therapy faces potential safety issue following a recent infant death in study Endpoints NewsNovartis got some more upbeat press earlier in the week when researchers on the Zolgensma gene therapy program outlined some updated biomarker data on ...
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Gene Therapy Cures Babies with "Bubble Boy" Disease - Genetic Engineering & Biotechnology News
Apr 19, 2019 | 11:00 amGene Therapy Cures Babies with "Bubble Boy" Disease Genetic Engineering & Biotechnology NewsEight infants with X-linked severe combined immunodeficiency (X-SCID) have been cured through an experimental gene therapy.
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Estimating the efficacy and cost of curative gene therapy for beta-thalassemia - EurekAlert
Apr 18, 2019 | 18:54 pmEstimating the efficacy and cost of curative gene therapy for beta-thalassemia EurekAlertNew Rochelle, NY, April 18, 2019--Gene therapy offers the promise of a cure for beta-thalassemia and a new study has shown that it is associated with fewer ...
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'Bubble boy' gene therapy results shoot Mustang Bio's stock up 200% - BioPharma Dive
Apr 18, 2019 | 17:57 pm'Bubble boy' gene therapy results shoot Mustang Bio's stock up 200% BioPharma DiveShares in Mustang Bio soared by as much as 200% Thursday after an experimental gene therapy it holds an exclusive license to proved successful in treating ...
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Two gene therapy approvals headline CBER's FY 2018 report - Endpoints News
Apr 18, 2019 | 15:53 pmTwo gene therapy approvals headline CBER's FY 2018 report Endpoints NewsThe FDA Center for Biologics Evaluation and Research (CBER) on Wednesday published its fiscal year 2018 report, highlighting two gene therapy approvals, ...
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Wotton replaces Gilman as CEO of cell, gene therapy startup Obsidian - FierceBiotech
Apr 18, 2019 | 14:41 pmWotton replaces Gilman as CEO of cell, gene therapy startup Obsidian FierceBiotechObsidian Therapeutics has named Paul Wotton as CEO. The appointment gives Obsidian a full-time CEO following a period in which Michael Gilman helmed the ...
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'Bubble Boy' Disease Helped By Advances In Gene Therapy : Shots - Health News - NPR
Apr 17, 2019 | 23:12 pm'Bubble Boy' Disease Helped By Advances In Gene Therapy : Shots - Health News NPRThe latest advance is not only encouraging news for patients with severe combined immunodeficiency. It's a test case for all those scientists working to develop ...
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Conservative thinkers urge caution on gene therapy - Politico
Apr 16, 2019 | 18:00 pmConservative thinkers urge caution on gene therapy PoliticoSupreme Court asks for admin input on PBM case — Achaogen bankruptcy points to challenges for superbug-focused companies.
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Dystrogen Therapeutics’ Gene Therapy Shows Promise for Huntington’s - Huntington's Disease News
Apr 16, 2019 | 09:00 amDystrogen Therapeutics’ Gene Therapy Shows Promise for Huntington’s Huntington's Disease NewsDYST 201, a gene therapy targeting only the mutated forms of the Huntington's disease gene, shows promising results, Dystrogen Therapeutics announced.
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Catalent to acquire gene therapy service firm Paragon - Chemical & Engineering News
Apr 15, 2019 | 23:56 pmCatalent to acquire gene therapy service firm Paragon Chemical & Engineering NewsInvestment in gene therapy capacity has exploded. April 2019. Catalent agrees to pay $1.2 billion for Paragon Bioservices. March 2019. Thermo Fisher buys ...
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Catalent to buy Paragon for $1.2B as gene therapy demand grows - BioPharma Dive
Apr 15, 2019 | 18:08 pmCatalent to buy Paragon for $1.2B as gene therapy demand grows BioPharma DiveCatalent is making a bid to strengthen its position as a contracted developer and manufacturer of gene therapies by acquiring Paragon Bioservices for $1.2 ...
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Gene Therapy Was Hailed as a Revolution. Then Came the Bill - Bloomberg
Apr 7, 2019 | 09:00 amGene Therapy Was Hailed as a Revolution. Then Came the Bill BloombergDozens of revolutionary gene therapies that mend faulty strands of DNA are on their way, bringing the power to eliminate lethal childhood diseases, rare blood ...
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