Breaking Gene Therapy News

Newt Gingrich: Don't let confusion and fear block promising genetic therapy treatments - Fox News

Dec 7, 2018 | 21:48 pm

Newt Gingrich: Don't let confusion and fear block promising genetic therapy treatments Fox NewsOver the past three decades, I have consistently spoken about the enormous potential of biomedical breakthroughs that could solve many of our pressing public ...

Orchard's Gene Therapy for Rare Immune Disease Works for Over a Year - Labiotech.eu

Dec 7, 2018 | 17:27 pm

Orchard's Gene Therapy for Rare Immune Disease Works for Over a Year Labiotech.euA single dose of a gene therapy developed by Orchard Therapeutics can restore immune function for at least a year in patients with X-linked chronic ...

Cell And Gene Therapy Logistics Requires Early Planning - Scrip

Dec 7, 2018 | 12:26 pm

Cell And Gene Therapy Logistics Requires Early Planning ScripIt has become standard practice for manufacturing to get early attention in the cell and gene therapy development, but logistics is often not considered until ...

Exclusive: Orchard CEO Touts Transformative Power of Gene Therapy Following ASH Data Presentation - BioSpace

Dec 6, 2018 | 21:15 pm

Exclusive: Orchard CEO Touts Transformative Power of Gene Therapy Following ASH Data Presentation BioSpaceThe word transformative is not used lightly by Orchard Therapeutics Chief Executive Officer Mark Rothera. He has seen the lives of children born with rare ...

XyloCor closes $17M Series A round to develop gene therapy for refractory angina - MedCity News

Dec 6, 2018 | 19:09 pm

XyloCor closes $17M Series A round to develop gene therapy for refractory angina MedCity NewsThe Philadelphia-based company has an IND open with the FDA and plans to begin its clinical trial in the first half of next year.

Gene therapy pioneers win $1 million Sanford Lorraine Cross Award - KSFY

Dec 5, 2018 | 22:05 pm

Gene therapy pioneers win $1 million Sanford Lorraine Cross Award KSFYTwo women with a vision to make the blind see are the recipients of the first ever Sanford Lorraine Cross award.

Voyager taps Brammer and Fujifilm for gene therapy development program - OutSourcing-Pharma.com

Dec 5, 2018 | 15:15 pm

Voyager taps Brammer and Fujifilm for gene therapy development program OutSourcing-Pharma.comThe clinical-stage gene therapy company Voyager Therapeutics has entered into collaborations with Brammer Bio and Fujifilm Diosynth Biotechnologies to ...

Gene therapy process reversing sickle cell anaemia symptoms - Health Europa

Dec 5, 2018 | 09:58 am

Gene therapy process reversing sickle cell anaemia symptoms Health EuropaAfter over a decade of preclinical research and development, a new gene therapy process is reversing sickle cell anaemia symptoms in patients.

Sickle Cell Gene Therapy Makes Another Advance - webmd.com

Dec 4, 2018 | 22:50 pm

Sickle Cell Gene Therapy Makes Another Advance webmd.comThe therapy targets the genetic flaw that causes sickle cell. In a small group of patients, researchers said the therapy appears safe and effective enough to keep ...

Gene therapy for blood disorders - EurekAlert

Dec 4, 2018 | 17:39 pm

Gene therapy for blood disorders EurekAlertDelivering gene-regulating material to cells that live deep in our bone marrow and direct the formation of blood cells. That would be a major step forward in gene ...

ASH18: Bluebird's gene therapy progress shadowed by MDS case - BioPharma Dive

Dec 4, 2018 | 16:51 pm

ASH18: Bluebird's gene therapy progress shadowed by MDS case BioPharma DiveBluebird bio can say with more conviction that tweaks made to its LentiGlobin gene therapy are bearing fruit, unveiling Monday updated trial results with longer ...

Niosomes, efficient DNA delivery vehicles for gene therapy of the central nervous system - EurekAlert

Dec 4, 2018 | 16:12 pm

Niosomes, efficient DNA delivery vehicles for gene therapy of the central nervous system EurekAlertGene therapy is a technique that is rapidly expanding and developing owing to the huge potential is has for therapeutic purposes. It basically consists of ...

NIH researcher presents encouraging results for gene therapy for severe sickle cell disease - National Institutes of Health

Dec 4, 2018 | 13:47 pm

NIH researcher presents encouraging results for gene therapy for severe sickle cell disease National Institutes of HealthA scientist from the National Institutes of Health will present promising, early results from a human clinical trial testing a novel gene replacement therapy in ...

Bluebird's gene therapy improved outcomes for patients in clinical trial - STAT

Dec 4, 2018 | 03:26 am

Bluebird's gene therapy improved outcomes for patients in clinical trial STATBoth Bluebird and Global Blood Therapeutics are seeking to take advantage of flexibility at the FDA and a desire to see new treatments reach the market.

Early clinical trial data show gene therapy reversing sickle cell anemia: Treatment uses reduced-intensity preconditioning to enhance its global transportability - Science Daily

Dec 4, 2018 | 03:26 am

Early clinical trial data show gene therapy reversing sickle cell anemia: Treatment uses reduced-intensity preconditioning to enhance its global transportability Science DailyAfter over a decade of preclinical research and development, a new gene therapy treatment for sickle cell anemia (SCA) is reversing disease symptoms in two ...

Gene therapy shows long-term activity in severe hemophilia B - Healio

Dec 3, 2018 | 21:55 pm

Gene therapy shows long-term activity in severe hemophilia B HealioSAN DIEGO — Patients with severe hemophilia B demonstrated stable therapeutic expression of the factor IX gene over an 8-year period without late toxicities ...

Novel Gene Therapy Promising for Sickle Cell Disease - Rare Disease Report

Dec 3, 2018 | 19:55 pm

Novel Gene Therapy Promising for Sickle Cell Disease Rare Disease ReportThe therapy attempts to restore fetal hemoglobin production.

Misfortune strikes a Bluebird patient, highlighting risks of gene therapy - STAT

Dec 2, 2018 | 16:35 pm

Misfortune strikes a Bluebird patient, highlighting risks of gene therapy STATSAN DIEGO — People get excited about gene therapy for the potential to cure some pretty horrible diseases, but the safety risks that patients take on with the ...

Autologous gene therapy shows promise for sickle cell disease - Healio

Dec 2, 2018 | 11:45 am

Autologous gene therapy shows promise for sickle cell disease HealioSAN DIEGO — An adult with sickle cell disease responded positively to autologous gene therapy, providing the first proof that this approach could be effective ...

Parkinson's Gene Therapy Wires New Brain Circuits - WebMD

Nov 28, 2018 | 09:00 am

Parkinson's Gene Therapy Wires New Brain Circuits WebMDIn a new study, gene therapy did not change the abnormal brain circuitry of Parkinson's disease. Instead, it essentially rewired a small area of the brain, ...

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