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New and Updated Clinical Gene Therapy Trials
Gene therapy studies updated or received in the last 30 days at ClinicalTrials.gov. Only open studies, recruiting or not yet recruiting, are shown found by a search using the keyword: "gene therapy OR gene transfer OR virus delivery"
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NG101 AAV Gene Therapy in Subjects With Wet Age-Related Macular Degeneration
09 August 2023Condition: Age-Related Macular DegenerationIntervention: Genetic: NG101 AAV gene therapySponsors: Neuracle Genetics, Inc; ORA, Inc.Recruiting
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An Expanded Clinical Study Evaluating the AAV2-RPE65 Gene Therapy(LX101) in Patients With LCA
05 September 2023Condition: To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)Intervention: Drug: LX101Sponsor: Shanghai General Hospital, Shanghai Jiao Tong University School of MedicineNot yet recruiting
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A Study to Evaluate the Efficacy and Safety of Factor IX Gene Therapy With PF-06838435 in Adult Males With Moderately Severe to Severe Hemophilia B
04 March 2019Condition: Hemophilia BIntervention: Biological: PF-06838435/ fidanacogene elaparvovecSponsor: PfizerRecruiting
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Liver Biopsy Following Gene Therapy For Hemophilia
06 July 2023Conditions: Hemophilia A; Hemophilia BIntervention: Procedure: Liver BiopsySponsor: St. Jude Children's Research HospitalNot yet recruiting
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Gene Transfer Clinical Trial for Krabbe Disease
05 January 2021Condition: Krabbe DiseaseIntervention: Biological: FBX-101Sponsor: Forge Biologics, IncRecruiting
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Follow-Up Study of Subjects Previously Enrolled in Poxviral Vector Gene Transfer Studies
22 March 2007Conditions: Prostate Cancer; Liver Cancer; Breast Cancer; Colon Cancer; Lung CancerIntervention: Sponsor: National Cancer Institute (NCI)Recruiting
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AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
20 January 2023Condition: Duchenne Muscular DystrophyIntervention: Genetic: RGX-202Sponsor: REGENXBIO Inc.Recruiting
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A Study of AAV9 Gene Therapy in Participants With Canavan Disease
10 August 2021Condition: Canavan DiseaseIntervention: Biological: AAV9 BBP-812Sponsor: Aspa TherapeuticsRecruiting
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Long-Term Follow-up of Gene Therapy for APOE4 Homozygote Alzheimer's Disease
01 June 2022Condition: Alzheimer DiseaseIntervention: Biological: LX1001Sponsor: Lexeo TherapeuticsRecruiting
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Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients
13 June 2023Condition: SMA IIIntervention: Genetic: GC101Sponsor: GeneCradle IncRecruiting
Clinical Trial Information
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Info ClinicalTrials.gov
Clinical gene therapy trials recently received at ClinicalTrials.gov database.
The U.S. National Institutes of Health, through its National Library of Medicine, has developed ClinicalTrials.gov to provide patients, family members and members of the public current information about clinical research studies. The database is a registry of federally and privately supported clinical trials conducted in the United States and around the world. ClinicalTrials.gov gives you information about a trial's purpose, who may participate, locations, and phone numbers for more details.
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Latest clinical trials |
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Search clinical trials |
The U.S. National Institutes of Health, through its National Library of Medicine, has developed ClinicalTrials.gov to provide patients, family members and members of the public current information about clinical research studies. The database is a registry of federally and privately supported clinical trials conducted in the United States and around the world. ClinicalTrials.gov gives you information about a trial's purpose, who may participate, locations, and phone numbers for more details.
Participate in Trial
Are you a patient and considering to participate in a clinical gene therapy trial? Your doctor may be an excellent resource to help identify clinical trials for a particular disease. There are a number of online resources that can also assist in locating clinical trials that are accepting patients:
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ClinicalTrials.gov |
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Cancer.gov |
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CenterWatch |
When looking for a clinical trial, remember to make sure the trial is appropriate for the disease. Most trials also specify an age range for the participants. Additional eligibility requirements must also be met, but these will vary depending on the individual study. Contact the health professionals if they are not listed. It is always best to discuss these issues before you travel to gene therapy center. More clinical trial information.
Be aware that Gene Therapy Net is not intended to replace or constitute the giving of medical treatments or advice.