News-Medical.Net Gene Therapy News
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Multi-million government fund given to 21 projects to propel innovation across the UK
Sep 17, 2021 | 01:49 amRegulators are clearing the runway for drones to transport vaccines and other live-saving drugs, in a ground-breaking venture funded by government.
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Novel cell reprogramming offers a promising therapeutic strategy to slow down glioblastomas
Sep 16, 2021 | 14:59 pmGliomas are the most common primary brain tumors in adults. Among them, high-grade glioblastomas (GBMs) are particularly known to be notoriously aggressive and invasive, which makes it challenging to treat them. The disease rapidly progresses to an advanced stage in a short span of time, and the survival of such patients is often dismal.
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Study pinpoints a potential pathway for treating epileptic seizures in patients with autism
Sep 16, 2021 | 02:39 amAutism affects about 2% of children in the United States, and about 30% of these children have seizures. Recent large-scale genetic studies revealed that genetic variants in a sodium channel, called voltage-gated sodium channel Nav1.2, is a leading cause of autism.
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First rat model recapitulates all disabling alterations experienced by patients with Morquio A disease
Sep 12, 2021 | 19:15 pmA research team from the Universitat Autònoma de Barcelona has generated the first rat model recapitulating all disabling alterations experienced by patients with Mucopolysaccharidosis type IVA, also known as Morquio A disease.
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New gene-delivering workhorse could make gene therapy safer, more effective for muscle diseases
Sep 10, 2021 | 05:24 amGenetic muscle diseases lead to progressive muscle wasting and often early death, with few treatment options and no cure.
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Researchers develop the smallest CRISPR to date for genome editing
Sep 5, 2021 | 04:41 amA compact and efficient CRISPR-Cas system, named CasMINI, could be broadly useful for cell-engineering and gene-therapy applications because it is easier to deliver into cells. The findings appear in a study publishing September 3 in the journal Molecular Cell.
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Stanford researchers engineer an efficient, multi-purpose, mini CRISPR system
Sep 4, 2021 | 07:59 amThe common analogy for CRISPR gene editing is that it works like molecular scissors, cutting out select sections of DNA. Stanley Qi, assistant professor of bioengineering at Stanford University, likes that analogy, but he thinks it's time to reimagine CRISPR as a Swiss Army knife.
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Targeting and inhibiting a protein could provide more effective treatment for brain cancer
Sep 1, 2021 | 03:27 amMcGill University researchers identify proteins that drive cancer stem cells. Targeting and supressing a particular protein called galectin1 could provide a more effective treatment for glioblastoma, in combination with radiation therapy.
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Aptamer Group and Bio-Works Technologies partner to enable improved solutions for gene therapy manufacturing
Aug 26, 2021 | 13:07 pmAptamer Group Ltd and Bio-Works Technologies AB today announce that they have entered into an agreement to co-develop a new affinity resin.
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Mission and money clash in nonprofit hospitals’ venture capital ambitions
Aug 24, 2021 | 14:12 pmCone Health, a small not-for-profit health care network in North Carolina, spent several years developing a smartphone-based system called Wellsmith to help people manage their diabetes.
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