News-Medical.Net Gene Therapy News
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Gene therapy can provide long-lasting therapeutic benefit in Huntington's disease
Jan 26, 2022 | 02:47 amGene therapy targeting the messenger RNA (mRNA) of the mutated huntingtin gene (HTT) can provide long-lasting therapeutic benefit in Huntington's disease after a single administration.
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Low-cost test could open new avenues for earlier diagnosis, treatment of rare genetic disorders
Jan 25, 2022 | 03:57 amA newly developed test to screen for three rare genetic disorders simultaneously in newborns was feasible, reliable and scalable, according to a new study.
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Novel gene therapy for diseased muscle fiber repair
Jan 24, 2022 | 17:55 pmIn this interview, News-Medical speaks to Dr. Jyoti K. Jaiswal about his latest research into gene therapies for limb-girdle muscular dystrophy 2B.
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Eikonoklastes completes a license to add novel gene therapy for treating neurodegenerative diseases
Jan 20, 2022 | 07:05 amEikonoklastes Therapeutics, a preclinical stage biopharmaceutical company, today announced it has completed a license with the University of California San Diego to add a novel gene therapy for the treatment of neurodegenerative diseases.
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Newly developed gene therapy can treat a severe form of epilepsy and prolong survival
Jan 20, 2022 | 06:16 amResearch from the University of Virginia School of Medicine suggests how a newly developed gene therapy can treat Dravet syndrome, a severe form of epilepsy, and potentially prolong survival for people with the condition.
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Study: Nearly 30% of people with blinding retinal disease can safely stop eye injection therapy
Jan 18, 2022 | 23:40 pmIn a preliminary study of 106 people with "wet" age-related macular degeneration, Johns Hopkins Medicine researchers report that as many as a third of those with the blinding retinal disease may someday be able to safely stop eye injection therapy without further vision loss.
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Big Tuna and automated buffer exchange: An interview with Unchained Labs
Jan 7, 2022 | 12:32 pmIn this interview, AZoNetwork speaks with Joe Barco, the Senior Director of Workflow Marketing at Unchained Labs, about the benefits of automated buffer exchange with Big Tuna.
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New study links anxiety and PTSD to increased myelin in brain's gray matter
Jan 7, 2022 | 00:22 amA recent study links anxiety behavior in rats, as well as post traumatic stress disorder (PTSD) in military veterans, to increased myelin - a substance that expedites communication between neurons - in areas of the brain associated with emotions and memory.
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New gene therapy addresses primary cellular deficit associated with limb-girdle muscular dystrophy 2B
Jan 5, 2022 | 04:05 amChildren's National Hospital experts developed a new pre-clinical gene therapy for a rare disorder, known as limb-girdle muscular dystrophy (LGMD) 2B, that addresses the primary cellular deficit associated with this disease.
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Structural blueprint of nanoparticles developed to target neutrophils responsible for acute lung inflammation
Dec 28, 2021 | 08:07 amThe COVID-19 pandemic highlighted the devastating impact of acute lung inflammation (ALI), which is part of the acute respiratory distress syndrome (ARDS) that is the dominant cause of death in COVID-19.
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