Gene Therapy Net Newsletter |
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News: Gene therapy eyedrops restored a boy's sight. Similar treatments could help millions
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Dr. Alfonso Sabater pulled up two photos of Antonio Vento Carvajal’s eyes. One showed cloudy scars covering both eyeballs. The other, taken after months of gene therapy given through eyedrops, revealed no scarring on either eye. Antonio, who's been legally blind for much of his 14 years, can see again. The teen was born with dystrophic epidermolysis bullosa, a rare genetic condition that causes blisters all over his body and in his eyes. But his skin improved when he joined a clinical trial to test the world’s first topical gene therapy. That gave Sabater an idea: What if it could be adapted for Antonio's eyes?
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We are thrilled to reveal the updated GeneTherapyNet.com – your go-to destination for the latest in gene therapy innovation! Our revamped design offers a seamless and intuitive experience, giving you instant access to essential insights into gene therapy breakthroughs. From foundational knowledge to real-life success stories and ongoing clinical trials, our curated content covers it all. Join our vibrant community of experts, engage in insightful discussions, and stay informed about key events shaping the field. Embark on an inspiring journey at www.genetherapynet.com to witness firsthand the incredible potential of gene therapy.
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Conference: Cell & Gene Therapy Manufacturing & Commercialization US
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World renowned leaders share the latest bioprocessing science and technologies to improve manufacturing scalability, cost, and quality to increase access to patients in rare diseases and beyond at the Cell & Gene Therapy Manufacturing & Commercialization US conference (19-21 September). Register by this Friday, August 18 to lock in the early bird rates for our All Access and Exhibition Visitor Passes. Also, be sure to register by this Friday to gain early access to the ConnectMe conference app that allows you to view the attendee list, pre-schedule meetings and connect with exhibitors before you arrive in Boston
Register now…
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Conference: BioProcess International
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Access the science, technologies and contacts you need to improve efficiencies across all phases of biopharmaceutical development and production at the BioProcess International conference (19-21 September). Register by this Friday, August 18 to lock in the early bird rates for our All Access and Exhibition Visitor Passes.
Register now…
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Conference: 4th Annual Gene Therapy for Ophthalmic Disorders Summit
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The 4th Annual Gene Therapy for Ophthalmic Disorders Summit (October 3-5, 2023 | Boston, MA) is the industry-leading, industry-focused forum for learning how to validate novel administration routes to the eye, extrapolate effectively from preclinical models to inform safety and efficacy and define relevant endpoints for clinical trials. Across 3 days of in-depth case studies, new data, and focused group discussions, hear from and engage with the likes of Janssen, Adverum Biotechnologies, Spark Therapeutics, SparingVision, AbbVie, and the RD Fund. As well as leveraging insights from these talks and panels: participate in breakout discussions, utilize Q&A time built into talks, and meet and learn from ophthalmic gene therapy leaders during our 5+ hours of dedicated networking time.
Register now…
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Conference: Biomarkers US 2023
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Gain a US perspective on the latest technologies and novel biomarkers driving forward translational research and precision medicine at Oxford Global’s 7th Annual Biomarkers US 2023 conference (12-13 October). The event brings together over 300 visionary leaders to network about the latest innovations in the field. Meet key decision makers representing leading pharma, biotech, and academic organisations working in the biomarker industry across multiple therapeutic areas.
Register now…
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Conference: Medical Affairs Summit
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The Medical Affairs Summit is scheduled to take place on 12 - 13 October 2023 at the luxurious Encore Boston Harbor in Boston, MA, US. The event brings together key Clinical Trial Executives representing pharmaceutical industries in the Americas. The Summit offers a highly focused and interactive platform for attendees to address core concerns and find solutions tailored to their specific needs. The Summit offers the opportunity for one-on-one business meetings, which allows sponsors to connect with key decision-makers in the industry. This can be instrumental in forging precious partnerships. This is an unparalleled opportunity for extensive networking among industry peers during one-on-one business meetings, event meals, cocktail receptions and leisure entertainment.
Register now…
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Conference: 2nd Innate Killer Europe Summit
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The 2nd Innate Killer Summit Europe (17-19 October) gathers 80+ key European Gamma Delta T, NK, iNKT, neutrophil, and macrophage developers in October to chase the holy grail of efficacious, off-the-shelf, solid tumour immunotherapies through effective and scalable engineering, engager and combination strategies that promote safe, potent and persistent innate immune therapies following application.
Register now…
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Conference: World Drug Safety Congress Americas 2023
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The World Drug Safety Congress Americas (18-19 October) will bring together hundreds of top leaders and stakeholders in biopharma to discuss the key challenges they are facing in pharmacovigilance and device safety. Explore strategies in data management & signal detection, showcase how AI & machine learning have improved PV processes, discuss the challenges creating a PV strategy for advanced therapies, and collaborate on medical device safety strategies. This conference is the largest commercial gathering of PV professionals in the world.
Register now…
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Conference: CRISPR-Based Therapy Analytical Development Summit
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CRISPR has opened the floodgates for a new era of gene editing therapies, promising to transform genetic disease treatments. With a well-established early field of genomics research, drug developers and researchers aim to establish the next-generation CRISPR toolkit, including Cas nucleases, base & prime editing technologies, and innovative delivery platforms.
The 3rd CRISPR 2.0 Summit will take place 28-30 November in Boston to showcase the latest innovations by uncovering how the next generation of CRISPR tools are radically enhancing efficacy, minimizing off-target effects & enabling efficient tissue-specific delivery to help you progress your program into and through the clinic.
Don't miss this opportunity to hear from 27+ expert speakers and network with 120+ key players in the space.
Register now…
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Upcoming conferences and meetings
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- 29 - 31 August 2023 - 3rd Inner Ear Disorders Therapeutics Summit - Gene & Cell Therapies - Boston, MA
- 29 - 31 August 2023 - mRNA Analytical Development Summit Europe - Berlin, Germany
- 29 - 31 August 2023 - Gene Therapy Potency Summit - Boston, MA
- 29 - 31 August 2023 - 2nd Next-Generation Lipid-Based Nanoparticle Delivery Summit - Boston, MA
- 29 August - 1 September 2023 - 8th CAR-TCR Summit - Boston, MA
- 30 - 31 August 2023 - Viral Vector Formulation & Process Development Summit Europe - Amsterdam, Netherlands
- 5 - 7 September 2023 - 4th Annual Gene Therapy Immunogenicity Summit - Boston, MA
- 5 - 7 September 2023 - 5th Exosome Based Therapeutic Development Summit - Gene Therapies - Boston, MA
- 6 - 7 September 2023 - RNA Leaders USA Congress - Boston, MA
- 12 - 14 September 2023 - 3rd Annual Mitochondria-Related Drug Dev. Summit - Gene Therapies - Boston, MA
- 18 - 21 September 2023 - Cell & Gene Therapy Manufacturing & Commercialization US - Boston, MA
- 18 - 21 September 2023 - BioProcess International - ATMP - Boston, MA
- 19 September 2023 - Cell Therapy Analytics Online Symposium 2023 - Online event
- 19 - 21 September 2023 - 2nd Cell Therapy Analytical Development Europe - Amsterdam, The Netherlands
- 25 - 27 September 2023 - Viral Vector Characterization & Analytical Development - Boston, MA
- 27 - 29 September 2023 - Smart Bioprocessing & Pharma 4.0 Summit - Cell & Gene Therapies - Berlin, Germany
- 3 – 5 October 2023 - 4th Annual Gene Therapy for Ophthalmic Disorders Summit - Boston, MA
- 12 – 13 October 2023 - Medical Affairs Summit - Boston, MA
- 12 - 13 October 2023 - Biomarkers US 2023 - San Diego, CA
- 17 – 19 October 2023 - 2nd Innate Killer Europe Summit - London, UK
- 18 – 19 October 2023 - World Drug Safety Congress Americas 2023 - Boston, MA
- 24 – 27 October 2023 - Annual Congress of the European Society of Gene and Cell Therapy - Brussels, Belgium
- 30 October - 1 November 2023 - TIDES Europe 2023 - Oligonucleotide and Peptide Therapeutics - Amsterdam
- 30 October - 1 November 2023 - CRISPR-Based Therapy Analytical Development Summit - Boston, MA
- 31 October - 2 November 2023 - 14th World Orphan Drug Congress Europe - Barcelona, Spain
- 6 - 9 November 2023 - 5th Gene Therapy for Neurological Disorders Summit - Boston, MA
- 7 - 8 November 2023 - Cell Series UK 2023 - London, UK
- 14 - 15 November 2023 - Precision Oncology Europe 2023 - Berlin, Germany
- 14 - 15 November 2023 - Biomarkers Europe 2023 - Berlin, Germany
- 16 - 17 November 2023 - Global Bioprocessing Summit - Gene & Cell Therapies - Berlin, Germany
- 27 - 30 November 2023 - 5th Annual Gene Therapy Analytical Development Summit 2023 - Boston, MA
- 28 - 30 November 2023 - Cell Therapy for Autoimmune Disease Summit - Philadelphia, PA
- 4 – 7 December 2023 - Cell & Gene Therapy Manufacturing & Commercialization Europe - Dublin, Ireland
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